Facebook
Instagram
Twitter
YouTube
RSS Feed
LinkedIn
Flickr
California Institute for Regenerative Medicine
For Researchers
FUNDING OPPORTUNITIES
Information for Applicants
All Funding Opportunities
COVID-19
Discovery
Translational
Clinical
Infrastructure
Education
Previous Funding Opportunities
GRANTS
Active Awards Portfolio Dashboard
CIRM Grants
Managing Your Grant
CIRM Grantees
CIRM-Funded Institutions
CIRM Funding Commitments
Stem Cell Grant Regulations
CLINICAL RESOURCES
CIRM Funded Clinical Trials
Alpha Stem Cell Clinics
Cell and Gene Therapy Center
Collaborative Funding Partnerships
RESEARCH RESOURCES
FAQs for CIRM Awards
Industry Alliance Program
iPSC Repository
Genomics Initiative
CIRM Publications
Grantee Publications
Webinars and Workshops
hESC Cell Lines
For Patients
Patient Resources
CIRM Funded Clinical Trials
Alpha Stem Cell Clinics
Stem Cell Champions
Disease Programs
Stories of Hope
CIRM Stem Cellar Blog
Stem Cell Videos
Stem Cell Basics
Stem Cell Key Terms
Creating New Types of Stem Cells
Accelerating Research Towards Cures
California: The Leader in Stem Cell Research
From Lab Bench to Bedside
Myths and Misconceptions About Stem Cell Research
Stem Cell Tourism
The Power of Stem Cells
Patient Toolbox
Get Involved
Talking About CIRM
Jargon-Free Glossary
Media Interviews
Delivering the Perfect Presentation
Moderating a Panel
Serving on a Panel
Participating in Clinical Trials
Our Impact
Impact
Active Awards Dashboard
Funding Clinical Trials
Return on Investment
Creating Jobs
Creating Infrastructure
Growing the Field
Strategic Plan
Education
Internship programs (Bridges & SPARK)
Education Portal
Training Tomorrow's Scientists
Community
Stem Cell Champions
Stem Cell Awareness Day
Get Involved
About CIRM
About Us
Our Mission
Leadership
Our History
2023 Annual Report
CIRM FAQ
Where CIRM funding goes
Job Opportunities
Contact Us
Governing Board
Public Meetings
CIRM Resources
Annual Report Archive
Strategic Plan
Funding Opportunities
Administrative Policies and Forms
News and Events
Newsroom
Meetings & Events
Public Meetings and Events
CIRM Board Meetings
Blog
Multimedia Resources
Podcast
Videos
Images
CIRM Fact Sheet
Logos
Contact Us
All CIRM Grants
Search Filters »
Disease Focus
(All)
aa Multiple Diseases (Centers & Resoures) (14)
Age-related macular degeneration (10)
Aging (21)
Alpha Thalassemia Major (3)
Alzheimer's Disease (35)
Amyotrophic Lateral Sclerosis (56)
Anemia (10)
Angelman Syndrome (1)
Arthritis (14)
Autism (22)
B cell cancers (12)
Beta Thalassemia (5)
Bladder or Urinary Tract Disorder (6)
Blood Cancer (70)
Blood Disorders (106)
Bone Marrow Transplant and Viral Infection (5)
Bone or Cartilage Disease (49)
Brain Cancer (30)
Brain Injury, hypoxic, ischemic (2)
Breast Cancer (7)
Canavan Disease (1)
Cancer (151)
Cartilage defect (4)
Colon Cancer (6)
Corneal Damage (7)
COVID-19 (23)
Cystic Fibrosis (2)
Cystinosis (3)
Danon Disease (1)
Dementia (4)
Developmental Disorders (18)
Diabetes (50)
Diabetic Wounds (1)
Duchenne Muscular Dystrophy (3)
Epidermolysis Bullosa (3)
Epilepsy (10)
Fertility (13)
Genetic Disorder (36)
Hearing Loss (11)
Heart Disease (100)
Heart disease associated with Duchenne muscular dystrophy (2)
Heart failure (10)
Hemophilia A (2)
HIV-related Lymphoma (2)
HIV/AIDS (42)
Huntington's Disease (36)
Hyper IgM Syndrome (2)
Hypertension, pulmonary arterial (1)
Immune Disease (53)
Incontinence (2)
Infectious Disease (53)
Inflammatory bowel disease (1)
Intellectual Disability (4)
Intervertebral disc degeneration (2)
Intestinal Disease (16)
IPEX Syndrome (5)
Kidney Disease (15)
Kidney Failure (14)
Leukemia (10)
Leukemia, Acute Myeloid (AML) (20)
Leukocyte Adhesion Deficiency (2)
Liver Disease (22)
Lung Cancer (6)
Lung Disease, Fibrosis (5)
Melanoma (11)
Metabolic Disorders (81)
Multiple Myeloma (7)
Multiple Sclerosis (9)
Muscle Injury (3)
Muscular Dystrophy (23)
N/A (441)
Neurological Disorders (285)
Neuropathy (5)
Osteoarthritis (6)
Osteonecrosis (3)
Other (15)
Ovarian Cancer (7)
Pancreatic Cancer (3)
Parkinson's Disease (48)
Pediatrics (69)
Prostate Cancer (7)
Pulmonary Hypertension (3)
Respiratory Disorders (26)
Retinitis Pigmentosa (11)
Rett's Syndrome (7)
Sanfilippo Syndrome/MPS III (2)
Sarcoma (3)
Severe Combined Immunodeficiency, Adenosine deaminase-deficient (ADA-SCID) (4)
Severe Combined Immunodeficiency, Artemis deficient (ART-SCID) (4)
Severe Combined Immunodeficiency, X-linked (X-SCID) (8)
Sickle Cell Disease (22)
Skeletal/Smooth Muscle disorders (41)
Skin cancer (2)
Skin Disease (17)
Solid Tumors (80)
Spina Bifida (4)
Spinal Cord Injury (40)
Spinal Muscular Atrophy (9)
Stroke (29)
Tendon/Ligament/Connective Tissue Injury or Disorder (2)
Thymic Disorder, 22q11 Deletion/DiGeorge (1)
Toxicity (7)
Trauma (11)
Traumatic Brain Injury (5)
Type 1 diabetes (20)
Vascular Disease (15)
Vision Loss (63)
Wounds, ulcers (1)
X-linked Chronic Granulomatous Disease (3)
Zika virus (2)
Institution
(All)
AcuraStem Inc. (1)
Adverum Biotechnologies (1)
Ali Nsair (1)
Alliance Forum Foundation (4)
American Association of Blood Banks (2)
Angiocrine Bioscience, Inc. (4)
Ankasa Regenerative Therapeutics, Inc. (2)
Aspen Neuroscience (1)
Aspera Biomedicines, Inc. (1)
Benjamin D. Yu (1)
Berkeley City College (2)
Biocom Institute (1)
BioEclipse Therapeutics INC. (1)
Biomedical Engineering Society (1)
BioTime, Inc. (1)
Bluebird Bio (1)
Boston Children’s Hospital (1)
Brain Mapping Foundation (1)
Brain Neurotherapy Bio (1)
BrainStorm Cell Therapeutics (1)
BrainXell Therapeutics (2)
Buck Institute for Age Research (9)
Cal Poly Corporation, an Auxiliary of California Polytechnic State University, San Luis Obispo (4)
Cal Poly Pomona Foundation (1)
Cal State Univ, Fullerton (4)
Cal State Univ, Long Beach (3)
Cal State Univ, Sacramento (3)
Cal State Univ, San Bernadino (4)
Caladrius Biosciences (2)
Calibr (3)
Calidi Biotherapeutics, Inc. (1)
California Institute of Technology (5)
California State University San Marcos Corporation (7)
California State University, Channel Islands (3)
Calimmune, Inc. (1)
Capricor, Inc (2)
Cedars-Sinai Medical Center (41)
Cellerant Therapeutics, Inc. (1)
Cellular Biomedicine Group, Inc. (1)
Cellular Dynamics International (1)
Celularity Inc. (1)
Chardan (1)
Charles R. Drew University of Medicine and Science (1)
Children’s Hospital of Los Angeles (17)
Children’s Hospital of Orange County (2)
Children’s Neurobiological Solutions (CNS) Foundation (1)
City College Of San Francisco (3)
City of Hope, Beckman Research Institute (54)
Combangio, Inc. (1)
Cytonus Therapeutics, Inc. (1)
Defined Bioscience, Inc. (1)
Elpida Therapeutics (1)
Escape Therapeutics, Inc (1)
Eureka Therapeutics, Inc. (1)
ExCellThera Inc. (1)
Excision BioTherapeutics (1)
Fate Therapeutics, Inc. (1)
Fluidigm Corporation (2)
Forty Seven Inc. (2)
FUJIFILM Cellular Dynamics (1)
Gamma Medica-Ideas, Inc. (1)
Genascence Corporation (1)
Geron Corporation (2)
Gladstone Institutes, J. David (37)
Global Genes (1)
GMR Epigenetics (1)
Gordon Research Conferences (3)
Greenstone Biosciences, Inc. (3)
HEALIOS NA, Inc. (1)
Humacyte, Inc. (2)
Human BioMolecular Research Institute (4)
Human Organ Project (1)
Humboldt State University Sponsored Programs Foundation (3)
Immune-Onc Therapeutics (1)
ImmunoCellular Therapeutics (1)
ImmunoVec (3)
Immusoft Corporation (2)
Int. Soc. for Cell Gene Ther. (1)
Intact Therapeutics, Inc. (1)
International Alliance for Biological Standardization (1)
International Society for Experimental Hematology (1)
International Society for Stem Cell Research (6)
International Symposium on Neural Regeneration, Inc. (1)
iPierian, Inc. (2)
IQVIA, Inc. (2)
Jackson Labs (1)
Jasper Therapeutics, Inc. (1)
jCyte, Inc (2)
JDRF International (2)
Juvena Therapeutics Inc. (1)
Keystone Symposia on Molecular and Cellular Biology (3)
La Jolla Institute for Allergy and Immunology (1)
Lineage Cell Therapeutics, Inc. (2)
Loma Linda University (2)
Ludwig Institute for Cancer Research (3)
Lundquist Institute for Biomedical Innovation at Harbor – UCLA Medical Center (3)
Mahzi Therapeutics (1)
MAX BioPharma, Inc. (1)
Medeor Therapeutics, Inc. (1)
Midwinter Conference of Immunologists (3)
Minutia, Inc. (1)
MiraCosta College (1)
Mohammad Pashmforoush (1)
Mosaic Event Management, Inc. (1)
MyoGene Bio LLC (1)
Nammi Therapeutics, Inc. (1)
Nanotools Bioscience (1)
Navega Therapeutics (1)
Neurona Therapeutics (4)
Nohla Therapeutics Inc (1)
Novoglia, Inc. (1)
Numerate, Inc. (1)
OCTANe Foundation for Innovation (1)
Ocular Research Symposia Foundation, Inc. (1)
OncoMed Pharmaceuticals, Inc. (1)
Orchard Therapeutics plc (1)
Organos, Inc. (1)
Ossium Health, Inc. (1)
Palo Alto Veterans Institute for Research (6)
Parkinson’s Institute (5)
Pasadena City College (3)
Pathways to Stem Cell Science (1)
Poseida Therapeutics, Inc. (2)
Rampart Bioscience (1)
RARE-X (1)
Ray Therapeutics, INC (2)
Regencor, Inc. (1)
Regenerative Patch Technologies LLC (1)
Rejuvenation Technologies, Inc. (1)
Research for Cure (1)
Reza Ardehali (1)
Rocket Pharmaceuticals, Inc. (2)
Rubedo Life Sciences Inc. (1)
Rumi Scientific CA (1)
RUNX1 Research Program (1)
Ryne Biotechnology (1)
Salk Institute for Biological Studies (23)
Samumed, LLC (1)
San Diego State University Foundation (5)
San Francisco State University (4)
SanBio, Inc. (1)
Sanford Burnham Prebys Medical Discovery Institute (27)
Sanford Consortium for Regenerative Medicine (8)
Sangamo BioSciences, Inc. (2)
Scaled Biolabs Inc. (1)
Scripps Health (5)
Scripps Research Institute (29)
Semma Therapeutics (1)
Siren Biotechnology, Inc. (1)
SJSU Research Foundation (3)
Solano Community College (1)
St. Jude Children’s Research Hospital (1)
Stanford University (172)
StemCells, Inc. (3)
Summit for Stem Cell Foundation (1)
Tachyon Therapeutics, Inc (1)
Tenaya Therapeutics, Inc. (1)
The American Society of Gene & Cell Therapy (1)
The Biomedical Engineering Society (1)
The Regents of the University of California on behalf of its Riverside Campus (9)
The Scintillon Institute (2)
The Stone Research Foundation for Sports Medicine and Arthritis (1)
The University Corporation at California State University, Northridge (4)
Tippi C. Mackenzie (1)
TriFoil Imaging, Inc. (1)
UCSF Benioff Children’s Hospital Oakland (8)
University of California, Berkeley (33)
University of California, Davis (76)
University of California, Irvine (69)
University of California, Los Angeles (156)
University of California, Merced (7)
University of California, San Diego (133)
University of California, San Francisco (119)
University of California, Santa Barbara (13)
University of California, Santa Cruz (16)
University of Southern California (52)
Vala Sciences, Inc. (1)
Vertuis Bio, Inc. (1)
ViaCyte, Inc. (9)
VistaGen Therapeutics, Inc. (1)
Vitabolus, Inc. (1)
Vitalant Research Institute (6)
VxBiosciences inc. (1)
Wake Forest University Health Sciences (1)
Western University of Health Sciences (1)
X-Therma Inc. (1)
Zenobia Therapeutics (1)
Program Type
(All)
Clinical (149)
Discovery (707)
Education (306)
Infrastructure (92)
Translation (146)
Grant Type
(All)
Accelerated Development Pathway I (1)
Accelerating Center (1)
Alpha Stem Cell Clinics (3)
Alpha Stem Cell Clinics Network Expansion (12)
Basic Biology I (12)
Basic Biology II (16)
Basic Biology III (27)
Basic Biology IV (28)
Basic Biology V (28)
Bridges (16)
Bridges (29)
Clinical Trial Stage Projects (3)
Clinical Trial Stage Projects (79)
COMPASS Training Grant (16)
Comprehensive Grant (29)
Conference (81)
Conference – Lung Regenerative Medicine Workshop (1)
Conference – Manage a Symposium on Pluripotent Stem Cell Manufacturing (1)
Conference – Manage The 2016 Bridges And SPARK Annual Meetings (1)
Conference – Manage The Bridges Annual Meeting (4)
Conference – Manage The SPARK Annual Meeting (6)
Conference – The 2016 Alpha Stem Cell Clinic Annual Symposium (1)
Conference – The 2017 Alpha Stem Cell Clinic Annual Symposium (1)
Conference – The 2018 Alpha Stem Cell Clinic Annual Symposium (1)
Conference – The 2019 Alpha Stem Cell Clinic Annual Symposium (1)
Conference – The Alpha Stem Cell Clinic Annual Symposium (2)
Conference – The 2020 Grantee Meeting (1)
Conference II (65)
Creativity Awards (9)
Cure Sickle Cell Initiative Clinical Trial Stage Projects (3)
Diagnostic Translational Research Projects (2)
Discovery Research Projects (12)
Discovery Research Projects (1)
Disease Team Planning (22)
Disease Team Research I (15)
Disease Team Therapy Development – Research (12)
Disease Team Therapy Development III (6)
Disease Team Therapy Planning I (19)
Early Translational from Disease Team Conversion (3)
Early Translational I (16)
Early Translational II (24)
Early Translational III (21)
Early Translational IV (14)
Foundation – Discovery Stage Research Projects (28)
Genomics Centers of Excellence Awards (R) (3)
hiPSC Derivation (1)
hPSC Repository (1)
Inception – Discovery Stage Research Projects (39)
iPSC Consortia Award (1)
Late Stage Preclinical Projects (39)
Major Facilities (12)
Manufacturing Network Grant (9)
Medical Device Translational Research Projects (1)
New Cell Lines (18)
New Faculty I (26)
New Faculty II (24)
New Faculty Physician Scientist (15)
Patent Assistance Fund Awards (8)
Preclinical Development Awards (7)
Progression Award – Discovery Stage Research Projects (8)
Quest – Discovery Stage Research Projects (144)
Research Leadership (14)
Research Training Grant (18)
Research Training II (17)
SEED Grant (74)
Shared Labs (34)
SPARK (18)
Strategic Partnership I (2)
Strategic Partnership II (1)
Strategic Partnership III Track A (2)
Targeted Clinical Development (1)
Therapeutic Translational Research Projects (73)
Therapeutic Translational Research Projects (1)
Tissue Collection for Disease Modeling (7)
Tool Translational Research Projects (6)
Tools and Technologies I (23)
Tools and Technologies II (20)
Tools and Technologies III (22)
Training Grant I-1 (8)
Training Grant I-2 (5)
Training Grant I-3 (3)
Translating Center (1)
Transplantation Immunology (20)
Human Stem Cell Use
(All)
Adult or Tissue Stem Cell (299)
Cancer Stem Cell (43)
Directly Reprogrammed Cell (11)
Embryonic Stem Cell (383)
iPS Cell (287)
N/A (405)
Other (11)
SCNT (2)
Somatic Cell (19)
Vital Research Opportunity (3)
Cell Line Generation
(All)
Adult or Tissue Stem Cell (60)
Cancer Stem Cell (12)
Directly Reprogrammed Cell (2)
Embryonic Stem Cell (52)
iPS Cell (126)
N/A (1048)
Other (9)
SCNT (2)
Collaborative Funder
(All)
Andalusia, Spain (1)
Australia (3)
Canada (2)
France (1)
Germany (10)
Japan (1)
NIH (3)
United Kingdom (3)
Victoria, Australia (6)
Award Status
(All)
Active (292)
Closed (1076)
Pre-Active (32)
Institution
Researcher name
Grant Type
Grant Title
Award Value
Stanford University
Jeffrey L Goldberg
Inception – Discovery Stage Research Projects
Embryonic Stem Cells for Corneal Endothelial Degeneration
$235,836
University of California, Los Angeles
Dr. Owen N Witte M.D.
Inception – Discovery Stage Research Projects
Identification of stem cell surface markers as potential therapeutic targets for advanced prostate cancer
$209,160
University of California, San Diego
Professor Alysson R Muotri
Inception – Discovery Stage Research Projects
Reverse transcriptase inhibitors as a novel therapeutic approach for neurological autoimmune disorders
$210,060
University of California, Los Angeles
Dr. April Pyle Ph.D.
Inception – Discovery Stage Research Projects
Novel Platforms to Enhance In Vivo Delivery of Skeletal Muscle Progenitor Cells from Human Pluripotent Stem Cells
$230,400
University of California, Los Angeles
Dr. Bennett G Novitch Ph.D.
Inception – Discovery Stage Research Projects
Organoid Modeling of Human Cortical Microcircuits
$208,916
Cedars-Sinai Medical Center
Professor Clive N Svendsen
Inception – Discovery Stage Research Projects
Blood Brain Barrier (BBB)-on-Chip: Development and validation of a novel iPS-based microfluidic model of the human BBB
$241,992
University of California, San Francisco
Dr. Holger F Willenbring
Inception – Discovery Stage Research Projects
Generation of bile duct-competent transplantable human liver organoids
$206,460
University of California, Los Angeles
Dr. Arjun Deb
Inception – Discovery Stage Research Projects
Targeting progenitors in scar tissue to reduce chronic scar burden
$230,400
University of California, Berkeley
Dr. Jacob Ellery Corn Ph.D
Inception – Discovery Stage Research Projects
Genome editing for causation and reversion of MPN-associated mutations in human hematopoietic stem cells
$235,800
Stanford University
Dr. Philip Arden Beachy PhD
Inception – Discovery Stage Research Projects
Curing bladder cancer by replacing corrupted urothelium with differentiated hES cells
$210,906
University of California, San Diego
Dionicio Siegel
Inception – Discovery Stage Research Projects
New Methods for the Chemical Expansion of Hematopoietic Stem and Progenitor Cells
$232,200
Stanford University
Dr. Bertha Chen
Inception – Discovery Stage Research Projects
Autologous iPSC-based therapy for radiation induced bladder injury
$235,836
University of California, Los Angeles
Dr. Thomas Carmichael M.D., Ph.D.
Inception – Discovery Stage Research Projects
iPS-Interneuron Transplantation for Neural Repair after Stroke
$229,396
University of California, San Diego
Dr. Karl J. Wahlin
Inception – Discovery Stage Research Projects
Microenvironment based optimization of retinal induction using CRISPR-CAS9 reporter pluripotent stem cells as an expandable source of retinal progenitors and photoreceptors.
$232,200
University of California, San Francisco
Andrew Stephen Brack
Inception – Discovery Stage Research Projects
Examining the efficacy of GDF11 antibody as a rejuvenator of aged human muscle stem cell capacity and muscle repair .
$180,000
Stanford University
Dr. Phillip Chung-Ming Yang
Inception – Discovery Stage Research Projects
Activation of patient-specific endogenous myocardial repair through the exosomes generated from the hypoxic iPSC-derived cardiomyocytes (iCMs).
$234,619
Cedars-Sinai Medical Center
Linda Cambier
Inception – Discovery Stage Research Projects
Exosomal Y-RNAs as mediators of bioactivity of cardiac-derived cell therapy
$181,063
Defined Bioscience, Inc.
Steven Douglas Rees
Tool Translational Research Projects
Development of a low-cost, clinical-grade iPS maintenance medium for enabling stem cell therapy manufacturing
$999,848
HEALIOS NA, Inc.
Tomonori Hosoya
Tool Translational Research Projects
Generation of human universal donor iPS cells
$999,989
University of California, Davis
Dr Jan A Nolta
Tool Translational Research Projects
T-Pure: Peripheral Blood Processing Tool for Point of Care CAR-T Manufacturing
$1,302,837
Greenstone Biosciences, Inc.
Paul D Pang
Tool Translational Research Projects
Cell Villages and Clinical Trial in a Dish with Pooled iPSC-CMs for Drug Discovery
$1,350,000
Organos, Inc.
Samuel Wall
Tool Translational Research Projects
Human iPSC-derived micro-heart muscles for high-throughput cardiac drug discovery
$1,119,382
Stanford University
Dr. Joseph C. Wu
Tool Translational Research Projects
A Novel, Robust and Comprehensive Predictive Tool Using Human Disease-Specific Induced Pluripotent Stem Cells for Preclinical Drug Screening
$975,000
University of California, Davis
Aijun Wang PhD
Medical Device Translational Research Projects
Living Synthetic Vascular Grafts with Renewable Endothelium
$3,082,579
University of California, San Francisco
Dr. Steven Mack PhD
Diagnostic Translational Research Projects
Development of a Noninvasive Prenatal Test for Beta-Hemoglobinopathies for Earlier Stem Cell Therapeutic Interventions
$633,014
UCSF Benioff Children’s Hospital Oakland
Dr. Henry A. Erlich Ph.D.
Diagnostic Translational Research Projects
Development of a Noninvasive Prenatal Test for Beta-Hemoglobinopathies for Earlier Stem Cell Therapeutic Interventions
$1,074,177
Ray Therapeutics, INC
Paul Bresge
Therapeutic Translational Research Projects
Optogenetic Therapy for Treatment of Geographic Atrophy
$3,998,930
University of California, San Francisco
Sarah Monica Knox
Therapeutic Translational Research Projects
Neurogenic hydrogel stimulation of stem cells to regenerate radiation-damaged salivary glands
$2,312,021
Siren Biotechnology, Inc.
Dr. Nicole K Paulk
Therapeutic Translational Research Projects
Development of an AAV gene therapy immunotherapy for the treatment of glioblastoma
$3,997,919
Cedars-Sinai Medical Center
Dr. Ahmed Gamal Ibrahim
Therapeutic Translational Research Projects
Noncoding RNA drug TY1 as a therapeutic candidate for scleroderma and systemic sclerosis
$2,590,224
University of California, San Diego
Dr Karen Christman
Therapeutic Translational Research Projects
Pro-regenerative infusible ECM biomaterial for treating acute myocardial infarction
$4,624,192
University of California, Los Angeles
Zulema Romero Garcia
Therapeutic Translational Research Projects
Adenine Base Editing for Autologous Hematopoietic Stem Cell Gene Therapy of CD3δ SCID
$5,966,928
University of California, Los Angeles
Dr. Donald B Kohn
Therapeutic Translational Research Projects
Hematopoietic Stem Cell Gene Editing for X-linked Agammaglobulinemia (XLA)
$4,309,973
University of California, San Diego
Dr. Eric D. Adler MD
Therapeutic Translational Research Projects
Ex Vivo Modified Hematopoietic Stem Cells to Treat Danon Disease
$5,180,389
University of California, Los Angeles
Dr. Gerald Lipshutz DDS, MD, MS
Therapeutic Translational Research Projects
Development of a Gene Therapy for the Treatment of Arginase Deficiency – Translating from Proof of Concept to Support Pre-IND Meeting
$5,266,504
City of Hope, Beckman Research Institute
Dr Michael A. Caligiuri
Therapeutic Translational Research Projects
Targeting multiple myeloma with BCMA-CAR NK cells expressing a GPRC5D-NKG2D bispecific antibody
$6,036,001
University of California, Los Angeles
Anthony J Aldave
Therapeutic Translational Research Projects
AAV Gene Therapy for Treating Congenital Hereditary Endothelial Dystrophy associated with Biallelic SLC4A11 Mutations
$4,338,166
ImmunoVec
Luke Riggan
Therapeutic Translational Research Projects
Hematopoietic Stem Cell Gene Therapy for Wiskott Aldrich Syndrome
$3,999,899
BrainXell Therapeutics
Dr. Emmanuel E Baetge
Therapeutic Translational Research Projects
Development of Autologous Cell Replacement Therapy for Parkinson’s Disease: Path to Personalized Treatment
$3,841,110
University of California, Los Angeles
Dr. Sophie X Deng
Therapeutic Translational Research Projects
Extracellular Vesicle-Based Therapy for Corneal Scars
$5,779,276
University of California, Los Angeles
Professor Scott G Kitchen
Therapeutic Translational Research Projects
Hematopoietic Stem/Progenitor Cell-Based Chimeric Antigen Receptor Gene Therapy for HIV Infection
$6,140,723
Rejuvenation Technologies, Inc.
John Ramunas
Therapeutic Translational Research Projects
Telomerase mRNA for short telomere related pulmonary fibrosis
$3,984,942
University of Southern California
Dr. Rongfu Wang
Therapeutic Translational Research Projects
Novel T cell receptor-STEM T cell immunotherapy in lung cancer
$5,689,540
Stanford University
Walter Park
Therapeutic Translational Research Projects
Enhanced Autologous Pancreatic Islet Transplantation and Survival for Diabetes Mellitus Therapy
$6,054,165
VxBiosciences inc.
Leor Weinberger
Therapeutic Translational Research Projects
Escape-Resistant Oligonucleotide Therapy (ONT) for Cytomegalovirus (CMV) Disease in Hematopoietic Stem-Cell and Solid-Organ Transplant Patients
$3,977,180
City of Hope, Beckman Research Institute
Dr Jianhua Yu
Therapeutic Translational Research Projects
Specific Targeting Hypoxia Metastatic Breast Tumor with Allogeneic Off-the-Shelf Anti-EGFR CAR NK Cells Expressing an ODD domain of HIF-1α
$6,036,002
Mahzi Therapeutics
Dr. Allyson Berent
Therapeutic Translational Research Projects
Development of a Gene Therapy for the Treatment of Pitt Hopkins Syndrome (PHS) – Translating from Animal Proof of Concept to Support Pre-IND Meeting
$3,800,760
University of California, Davis
Dr. William J Murphy
Therapeutic Translational Research Projects
Overcoming resistance to standard CD19-targeted CAR T using a novel triple antigen targeted vector
$3,869,061
University of California, San Diego
Stephanie Cherqui
Therapeutic Translational Research Projects
CRISPR/Cas9-mediated gene editing of Hematopoietic stem and progenitor cells for Friedreich’s ataxia
$4,846,579
University of Southern California
Preet M Chaudhary
Therapeutic Translational Research Projects
Next generation affinity-tuned CAR for prostate cancer
$5,805,144
« Previous
1
2
3
4
5
6
7
8
9
10
11
12
13
14
15
16
17
…
28
Next »