University of California, Los Angeles |
Dawn Ward |
Manufacturing Network Grant |
Enhancing California’s Manufacturing of Leading-Edge Cell & Gene Therapies |
$2,000,000 |
University of California, Los Angeles |
Steven Schwartz |
Late Stage Preclinical Projects |
Clinical Translation of Autologous Regenerative Pluripotent Stem Cell Therapy for Blindness |
$6,000,000 |
University of California, Los Angeles |
Scott Kitchen |
Therapeutic Translational Research Projects |
Hematopoietic Stem/Progenitor Cell-Based Chimeric Antigen Receptor Gene Therapy for HIV Infection |
$6,140,723 |
University of California, Los Angeles |
Sophie Deng |
Therapeutic Translational Research Projects |
Extracellular Vesicle-Based Therapy for Corneal Scars |
$5,779,276 |
University of California, Los Angeles |
Anthony Aldave |
Therapeutic Translational Research Projects |
AAV Gene Therapy for Treating Congenital Hereditary Endothelial Dystrophy associated with Biallelic SLC4A11 Mutations |
$4,338,166 |
University of California, Los Angeles |
Gay Crooks |
Foundation - Discovery Stage Research Projects |
Engineering pluripotent stem cells for universally available, off-the-shelf T cell therapies |
$1,352,753 |
University of California, Los Angeles |
Brigitte Gomperts |
Foundation - Discovery Stage Research Projects |
Overcoming barriers for airway stem cell gene therapy for Cystic Fibrosis |
$1,472,858 |
University of California, Los Angeles |
Kathrin Plath |
Foundation - Discovery Stage Research Projects |
Characterization and applications of human blastoids for understanding early human embryogenesis |
$1,402,137 |
University of California, Los Angeles |
William Lowry |
Foundation - Discovery Stage Research Projects |
Defining the source of dysfunction in monogenic Intellectual Disability Syndrome neurons |
$1,500,337 |
University of California, Los Angeles |
Frank Pajonk |
Quest - Discovery Stage Research Projects |
Development of novel small molecules against cancer stem cells in solid cancers |
$2,340,000 |
University of California, Los Angeles |
Gerald Lipshutz |
Quest - Discovery Stage Research Projects |
Gene Therapy for SLC6A8 Creatine Transporter Disorder |
$2,296,920 |
University of California, Los Angeles |
Richard Pietras |
Quest - Discovery Stage Research Projects |
Reversal of dysregulated myelopoiesis in breast cancers and cancer stem cells to boost antitumor immunotherapy |
$2,327,680 |
University of California, Los Angeles |
Song Li |
Quest - Discovery Stage Research Projects |
Vax-CT to promote formation of cancer-specific T memory stem cell for personalized cancer immunotherapy |
$2,267,714 |
University of California, Los Angeles |
Noah Federman |
Alpha Stem Cell Clinics Network Expansion |
Expansion of the Alpha Stem Cell and Gene Therapy Clinic at UCLA |
$8,000,000 |
University of California, Los Angeles |
Melissa Spencer |
Foundation - Discovery Stage Research Projects |
Engineering AAV capsids for transduction of neural and muscle stem cells |
$999,999 |
University of California, Los Angeles |
Tracy Johnson |
COMPASS Training Grant |
COMPASS: Accelerating Stem Cell Research by Educating and Empowering New Stem Cell Researchers |
$2,910,000 |
University of California, Los Angeles |
Donald Kohn |
Quest - Discovery Stage Research Projects |
Hematopoietic Stem Cell Gene Therapy for Alpha Thalassemia |
$1,177,739 |
University of California, Los Angeles |
Caroline Kuo |
Quest - Discovery Stage Research Projects |
Defining the Optimal Gene Therapy Approach of Human Hematopoietic Stem Cells for the Treatment of Dedicator of Cytokinesis 8 (DOCK8) Deficiency |
$1,386,232 |
University of California, Los Angeles |
Dinesh Rao |
Quest - Discovery Stage Research Projects |
Novel methods to eliminate cancer stem cells |
$1,384,347 |
University of California, Los Angeles |
Xian-Jie Yang |
Quest - Discovery Stage Research Projects |
Developing gene therapy for dominant optic atrophy using human pluripotent stem cell-derived retinal organoid disease models |
$1,345,691 |
University of California, Los Angeles |
Lili Yang |
Quest - Discovery Stage Research Projects |
Combating Ovarian Cancer Using Stem Cell-Engineered Off-The-Shelf CAR-iNKT Cells |
$1,404,000 |
University of California, Los Angeles |
Donald Kohn |
Therapeutic Translational Research Projects |
Autologous MPO Knock-Out Hematopoietic Stem and Progenitor Cells for Pulmonary Arterial Hypertension |
$4,751,297 |
University of California, Los Angeles |
Antoni Ribas |
Late Stage Preclinical Projects |
Skin regeneration and wound healing with a topical BRAF inhibitor |
$5,005,126 |
University of California, Los Angeles |
Song Li |
Quest - Discovery Stage Research Projects |
iPSC Extracellular Vesicles for Diabetes Therapy |
$1,354,928 |
University of California, Los Angeles |
Irene Llorente |
Therapeutic Translational Research Projects |
Clinical Translation of Allogenic Regenerative Cell Therapy for White Matter Stroke and Vascular Dementia |
$775,689 |
University of California, Los Angeles |
Arjun Deb |
Therapeutic Translational Research Projects |
Targeting stromal progenitors to prevent the development of heart failure |
$4,841,428 |
University of California, Los Angeles |
William Lowry |
Research Training Grant |
UCLA Training Program in Stem Cell Biology |
$5,000,000 |
University of California, Los Angeles |
Lili Yang |
Therapeutic Translational Research Projects |
HSC-Engineered Off-The-Shelf CAR-iNKT Cell Therapy for Multiple Myeloma |
$5,281,199 |
University of California, Los Angeles |
Cristina Puig Saus |
Therapeutic Translational Research Projects |
CAR-Tnm cell therapy for melanoma targeting TYRP-1 |
$5,904,462 |
University of California, Los Angeles |
Donald Kohn |
Quest - Discovery Stage Research Projects |
Hematopoietic Stem Cell Gene Therapy for X-linked Agammaglobulinemia |
$219,230 |
University of California, Los Angeles |
Stanley Carmichael |
Quest - Discovery Stage Research Projects |
Human-induced pluripotent stem cell-derived glial enriched progenitors to treat white matter stroke and vascular dementia. |
$250,000 |
University of California, Los Angeles |
Lili Yang |
Discovery Research Projects |
Battling COVID-19 Using Off-The-Shelf HSC-Engineered iNKT Cells |
$250,000 |
University of California, Los Angeles |
Song Li |
Discovery Research Projects |
Biomaterial vaccine to enhance the formation of SARS-CoV-2-specific T memory stem cells |
$149,916 |
University of California, Los Angeles |
Vaithilingaraja Arumugaswami |
Therapeutic Translational Research Projects |
COVID-19 Antiviral Therapy to Block Direct Cell Injury and Associated Tissue Damage |
$349,999 |
University of California, Los Angeles |
Caroline Kuo |
Progression Award - Discovery Stage Research Projects |
Evaluation of Gene Therapy Approaches for Autosomal Recessive Hyper IgE Syndrome Due to Mutations in DOCK8 |
$234,000 |
University of California, Los Angeles |
Brigitte Gomperts |
Discovery Research Projects |
Identifying a lead compound for COVID19 using high throughput screening with lung stem cell organoids |
$149,998 |
University of California, Los Angeles |
Gay Crooks |
Discovery Research Projects |
Stem cell-based rapid identification of SARS-CoV-2 T cell epitopes and T cell receptors for therapeutic use |
$126,692 |
University of California, Los Angeles |
Sophie Deng |
Clinical Trial Stage Projects |
Safety and Feasibility of Cultivated Autologous Limbal Stem Cells for Limbal Stem Cell Deficiency |
$10,301,486 |
University of California, Los Angeles |
Caroline Kuo |
Therapeutic Translational Research Projects |
Ex Vivo Gene Editing of Human Hematopoietic Stem Cells for the Treatment of X-Linked Hyper-IgM Syndrome |
$4,896,628 |
University of California, Los Angeles |
Yvonne Chen |
Therapeutic Translational Research Projects |
BCMA/CS1 Bispecific CAR-T Cell Therapy to Prevent Antigen Escape in Multiple Myeloma |
$3,176,805 |
University of California, Los Angeles |
Theodore Nowicki |
Clinical Trial Stage Projects |
Genetic Modification of Stem Cells and T cells to Activate the Immune System to Target Solid Tumors |
$4,230,000 |
University of California, Los Angeles |
Steven Schwartz |
Therapeutic Translational Research Projects |
Clinical Translation of Autologous Regenerative Cell Therapy for Blindness |
$5,068,026 |
University of California, Los Angeles |
Lili Yang |
Quest - Discovery Stage Research Projects |
Preclinical Development of An HSC-Engineered Off-The-Shelf iNKT Cell Therapy for Cancer |
$1,404,000 |
University of California, Los Angeles |
Steven Dubinett |
Clinical Trial Stage Projects |
A phase I trial of intratumoral administration of CCL21-gene modified dendritic cell (DC) combined with intravenous pembrolizumab for advanced NSCLC |
$10,955,315 |
University of California, Los Angeles |
John Adams |
Conference - The 2018 Alpha Stem Cell Clinic Annual Symposium |
Delivery of Stem Cell Therapeutics to Patients |
$60,000 |
University of California, Los Angeles |
Scott Kitchen |
Quest - Discovery Stage Research Projects |
Engineering Lifelong Cellular Immunity to HIV |
$1,701,178 |
University of California, Los Angeles |
April Pyle |
Quest - Discovery Stage Research Projects |
Identification and Generation of Long Term Repopulating Human Muscle Stem Cells from Human Pluripotent Stem Cells |
$2,148,519 |
University of California, Los Angeles |
Stanley Carmichael |
Quest - Discovery Stage Research Projects |
iPS Glial Therapy for White Matter Stroke and Vascular Dementia |
$2,086,130 |
University of California, Los Angeles |
Alireza Moshaverinia |
Inception - Discovery Stage Research Projects |
Gingival mesenchymal stem cells as a novel treatment modality for periodontal tissue regeneration |
$194,483 |
University of California, Los Angeles |
Caroline Kuo |
Quest - Discovery Stage Research Projects |
Targeted Gene Editing in the Treatment of X-Linked Hyper-IgM Syndrome |
$1,512,333 |
University of California, Los Angeles |
Gay Crooks |
Quest - Discovery Stage Research Projects |
Platform Technology for Pluripotent Stem Cell-Derived T cell Immunotherapy |
$965,636 |
University of California, Los Angeles |
Vaithilingaraja Arumugaswami |
Quest - Discovery Stage Research Projects |
Immunization strategies to prevent Zika viral congenital eye and brain disease |
$2,128,867 |
University of California, Los Angeles |
Song Li |
Conference II |
The 18th Annual UC System-Wide Bioengineering Symposium |
$25,000 |
University of California, Los Angeles |
John Chute |
Quest - Discovery Stage Research Projects |
Protein tyrosine phosphatase - sigma inhibitors for hematopoietic regeneration |
$2,115,735 |
University of California, Los Angeles |
Donald Kohn |
Clinical Trial Stage Projects |
Efficacy and safety of cryopreserved autologous CD34+ HSC transduced with EFS lentiviral vector encoding for human ADA gene in ADA-SCID subjects |
$10,156,925 |
University of California, Los Angeles |
Donald Kohn |
Clinical Trial Stage Projects |
Efficacy and safety of cryopreserved autologous CD34+ HSC transduced with EFS lentiviral vector encoding for human ADA gene in ADA-SCID subjects |
$5,827,000 |
University of California, Los Angeles |
April Pyle |
Quest - Discovery Stage Research Projects |
CRISPR/Cas9 nanoparticle enabled therapy for Duchenne Muscular Dystrophy in muscle stem cells |
$2,150,400 |
University of California, Los Angeles |
Sophie Deng |
Late Stage Preclinical Projects |
Regeneration of a Normal Corneal Surface by Limbal Stem Cell Therapy |
$4,244,211 |
University of California, Los Angeles |
Brigitte Gomperts |
Conference - Lung Regenerative Medicine Workshop |
Stem Cells for Lung Diseases - Overcoming Barriers to Find New Therapies |
$44,548 |
University of California, Los Angeles |
Stanley Carmichael |
Inception - Discovery Stage Research Projects |
iPS-Interneuron Transplantation for Neural Repair after Stroke |
$229,396 |
University of California, Los Angeles |
Arjun Deb |
Inception - Discovery Stage Research Projects |
Targeting progenitors in scar tissue to reduce chronic scar burden |
$230,400 |
University of California, Los Angeles |
Bennett Novitch |
Inception - Discovery Stage Research Projects |
Organoid Modeling of Human Cortical Microcircuits |
$208,916 |
University of California, Los Angeles |
April Pyle |
Inception - Discovery Stage Research Projects |
Novel Platforms to Enhance In Vivo Delivery of Skeletal Muscle Progenitor Cells from Human Pluripotent Stem Cells |
$230,400 |
University of California, Los Angeles |
Owen Witte |
Inception - Discovery Stage Research Projects |
Identification of stem cell surface markers as potential therapeutic targets for advanced prostate cancer |
$209,160 |
University of California, Los Angeles |
Peter Butler |
Therapeutic Translational Research Projects |
Personalized Cell Therapy for Diabetes |
$1,494,896 |
University of California, Los Angeles |
Lili Yang |
Therapeutic Translational Research Projects |
Stem Cell-Based iNKT Cell Therapy for Cancer |
$6,956,775 |
University of California, Los Angeles |
Donald Kohn |
Conference II |
Primary Immune Deficiency Treatment Consortium (PIDTC) Annual Scientific Workshop |
$29,807 |
University of California, Los Angeles |
Donald Kohn |
Clinical Trial Stage Projects |
A Phase I/II, Non Randomized, Multicenter, Open-Label Study of G1XCGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease |
$7,083,364 |
University of California, Los Angeles |
Hanna Mikkola |
Tools and Technologies III |
A suite of engineered human pluripotent stem cell lines to facilitate the generation of hematopoietic stem cells |
$1,382,400 |
University of California, Los Angeles |
James Dunn |
Tools and Technologies III |
Skin-derived precursor cells for the treatment of enteric neuromuscular dysfunction |
$1,044,423 |
University of California, Los Angeles |
Carla Koehler |
Tools and Technologies III |
A small molecule tool for reducing the malignant potential in reprogramming human iPSCs and ESCs |
$1,283,900 |
University of California, Los Angeles |
Leif Havton |
Tools and Technologies III |
Development of a Relevant Pre-Clinical Animal Model as a Tool to Evaluate Human Stem Cell-Derived Replacement Therapies for Motor Neuron Injuries and Degenerative Diseases |
$1,308,711 |
University of California, Los Angeles |
John Adams |
Alpha Stem Cell Clinics |
UCLA-UCI Alpha Stem Cell Clinic (ASCC) Consortium |
$8,680,000 |
University of California, Los Angeles |
John Chute |
Research Leadership |
Niche-Focused Research: Discovery & Development of Hematopoietic Regenerative Factors |
$4,645,297 |
University of California, Los Angeles |
Lili Yang |
Basic Biology V |
Differentiation of Human Hematopoietic Stem Cells into iNKT Cells |
$614,400 |
University of California, Los Angeles |
Denis Evseenko |
Basic Biology V |
Promoting survival and countering hypertrophy of pluripotent stem cell (PSC)-derived chondrocytes |
$411,330 |
University of California, Los Angeles |
Bennett Novitch |
Basic Biology V |
In vitro modeling of human motor neuron disease |
$1,147,114 |
University of California, Los Angeles |
Samantha Butler |
Basic Biology V |
Assessing the mechanism by which the Bone Morphogenetic Proteins direct stem cell fate |
$515,730 |
University of California, Los Angeles |
Donald Kohn |
Disease Team Therapy Development III |
Clinical Trial of Stem Cell Gene Therapy for Sickle Cell Disease |
$13,145,465 |
University of California, Los Angeles |
Dennis Slamon |
Disease Team Therapy Development III |
A Phase I dose escalation and expansion clinical trial of the novel first-in-class Polo-like Kinase 4 (PLK4) inhibitor, CFI-400945 in patients with advanced solid tumors |
$5,683,693 |
University of California, Los Angeles |
Dana Jones |
Conference |
7th CA/HSCI Junior PI Conference: Stem Cells 2.0 |
$2,500 |
University of California, Los Angeles |
Donald Kohn |
Early Translational IV |
Beta-Globin Gene Correction of Sickle Cell Disease in Hematopoietic Stem Cells |
$1,651,884 |
University of California, Los Angeles |
Gerald Lipshutz |
Early Translational IV |
Gene therapy-corrected autologous hepatocyte-like cells from induced pluripotent stem cells for the treatment of pediatric single enzyme disorders |
$1,801,629 |
University of California, Los Angeles |
Robert Reiter |
Early Translational IV |
Clinical Development of an N-cadherin Antibody to Target Cancer Stem Cells |
$4,075,668 |
University of California, Los Angeles |
Zack Jerome |
Early Translational IV |
Stem Cell Programming With Chimeric Antigen Receptors to Eradicate HIV Infection |
$4,925,166 |
University of California, Los Angeles |
Brigitte Gomperts |
Tissue Collection for Disease Modeling |
Using human induced pluripotent stem cells to improve our understanding of Idiopathic Pulmonary Fibrosis |
$811,231 |
University of California, Los Angeles |
Tatiana Segura |
Conference |
2013 Materials Research Society (MRS) Spring Meeting Symposium
"Design of Cell Instructive Materials" |
$4,000 |
University of California, Los Angeles |
Ali Nsair |
New Faculty Physician Scientist |
Human Induced Pluripotent Stem Cell-Derived Cardiovascular Progenitor Cells for Cardiac Cell Therapy. |
$2,316,894 |
University of California, Los Angeles |
Reza Ardehali |
New Faculty Physician Scientist |
Preclinical evaluation of human embryonic stem cell-derived cardiovascular progenitors in a large animal model |
$2,930,388 |
University of California, Los Angeles |
Kathrin Plath |
Basic Biology IV |
Understanding the status of the X chromosomes in human ESCs and preimplantation embryos |
$1,382,400 |
University of California, Los Angeles |
Owen Witte |
Basic Biology IV |
Trop2 dependent and independent mechanisms of self-renewal in human cancer stem cells |
$1,254,960 |
University of California, Los Angeles |
Antoni Ribas |
Disease Team Therapy Development - Research |
Genetic Re-programming of Stem Cells to Fight Cancer |
$14,144,221 |
University of California, Los Angeles |
Stanley Nelson |
Early Translational from Disease Team Conversion |
Combination therapy to Enhance Antisense Mediated Exon Skipping for Duchenne Muscular Dystrophy |
$1,823,545 |
University of California, Los Angeles |
Antoni Ribas |
Disease Team Therapy Planning I |
Genetic Re-programming of Stem Cells to Fight Cancer |
$97,785 |
University of California, Los Angeles |
Stanley Nelson |
Disease Team Therapy Planning I |
Combination therapy to Enhance Antisense Mediated Exon Skipping for Duchenne Muscular Dystrophy |
$68,947 |
University of California, Los Angeles |
Martina Wiedau-Pazos |
Conference |
California ALS Summit 2011 |
$13,300 |
University of California, Los Angeles |
Adele Rennie |
Patent Assistance Fund Awards |
Patent Assistance Fund - UCLA |
$84,973 |
University of California, Los Angeles |
Ali Nsair |
Basic Biology III |
Characterization and Engineering of the Cardiac Stem Cell Niche |
$1,127,741 |
University of California, Los Angeles |
Kathrin Plath |
Basic Biology III |
Discovery of mechanisms that control epigenetic states in human reprogramming and pluripotent cells |
$1,364,598 |
University of California, Los Angeles |
William Lowry |
Basic Biology III |
Molecular determinants of accurate differentiation from human pluripotent stem cells |
$677,115 |