Funding Clinical Trials

Our Agency funds clinical trials testing promising stem cell or gene therapies for currently incurable diseases or disorders to help patients with unmet medical needs. For basic information about stem cell trials, visit our Clinical Trials 101 page. For a list of clinical trials that are a result of early-stage CIRM grants click here.

108

CIRM-FUNDED CLINICAL TRIALS

Disease AreasInvestigatorOrganizationPhaseTrial StatusTarget EnrollmentDetail
Immune Disease
Pediatrics
X-linked Chronic Granulomatous Disease
Dr. Mona AuYoung PhD University of California, Los Angeles Phase 1/2 Recruiting 16
Pediatrics
Sickle Cell Disease
Dr. Mona AuYoung PhD University of California, Los Angeles Phase 1 Active, not recruiting 4
Genetic Disorder
Immune Disease
Pediatrics
Severe Combined Immunodeficiency, Adenosine deaminase-deficient (ADA-SCID)
Dr. Donald B Kohn
Leslie Meltzer
Dr. Mona AuYoung PhD
University of California, Los Angeles
Orchard Therapeutics plc
Phase 2 Completed 10
Muscle Injury Peter C Belafsky University of California, Davis Phase 1/2 Recruiting 62
Immune Disease DR Jonathan Benjamin ImmPACT-Bio, Inc. Phase 1/2 Launching N/A
Cystinosis
Kidney Failure
Dr. Stephanie Cherqui University of California, San Diego Phase 1/2 Active, not recruiting 6
HIV/AIDS
Immune Disease
Steven G. Deeks University of California, San Francisco Phase 1/2 Recruiting 18
Developmental Disorders
Spina Bifida
Dr. Diana L. Farmer University of California, Davis Phase 2 Recruiting 55
Immune Disease
Severe Combined Immunodeficiency, X-linked (X-SCID)
Stephen Gottschalk St. Jude Children’s Research Hospital Phase 1/2 Suspended 28
Bone or Cartilage Disease
Hearing Loss
Intellectual Disability
Metabolic Disorders
Vision Loss
Dr Robert Hayes Immusoft Corporation Phase 1 Launching N/A
Arthritis
Osteoarthritis
Dr. Kristen A Johnson Calibr Phase 1 Completed 60
Neurological Disorders
Other
Prof. Olivia Kim-McManus University of California, San Diego Phase 1/2 Launching N/A
Pulmonary Hypertension
Vascular Disease
Dr. Michael I Lewis Cedars-Sinai Medical Center Phase 1/2 Completed 26
Immune Disease
Pediatrics
Severe Combined Immunodeficiency, X-linked (X-SCID)
Dr. Judith A Shizuru
Wendy Pang
Stanford University
Jasper Therapeutics, Inc.
Phase 1/2 Recruiting 40
Immune Disease
Leukocyte Adhesion Deficiency
Dr. Kinnari Patel Rocket Pharmaceuticals, Inc. Phase 1/2 Completed 9
Danon Disease
Pediatrics
Dr. Jonathan Schwartz Rocket Pharmaceuticals, Inc. Phase 2 Launching N/A
Solid Tumors Dr. Dennis J Slamon University of California, Los Angeles Phase 1 Completed 46
Lupus, Systemic Lupus Erythematosus (SLE) Dr Bob Valamehr Fate Therapeutics, Inc. Phase 1 Launching N/A
COVID-19
Respiratory Disorders
William van der Touw Celularity Inc. Phase 1/2 Unknown status 86
Blood Cancer
Solid Tumors
Dr. Irving L Weissman MD Stanford University Phase 1 Completed 88
Bladder or Urinary Tract Disorder James Yoo Wake Forest University Health Sciences Phase 1 Not yet recruiting 10
COVID-19
Respiratory Disorders
Prof. John A Zaia City of Hope, Beckman Research Institute Phase 1 Launching N/A