Funding Clinical Trials

Our Agency funds clinical trials testing promising stem cell or gene therapies for currently incurable diseases or disorders to help patients with unmet medical needs. For basic information about stem cell trials, visit our Clinical Trials 101 page. For a list of clinical trials that are a result of early-stage CIRM grants click here.

108

CIRM-FUNDED CLINICAL TRIALS

Disease Areas	Investigator	Organization	Phase	Trial Status	Target Enrollment
Immune Disease Pediatrics X-linked Chronic Granulomatous Disease	Dr. Mona AuYoung PhD	University of California, Los Angeles	Phase 1/2	Recruiting	16
Pediatrics Sickle Cell Disease	Dr. Mona AuYoung PhD	University of California, Los Angeles	Phase 1	Active, not recruiting	4
Genetic Disorder Immune Disease Pediatrics Severe Combined Immunodeficiency, Adenosine deaminase-deficient (ADA-SCID)	Dr. Donald B Kohn Leslie Meltzer Dr. Mona AuYoung PhD	University of California, Los Angeles Orchard Therapeutics plc	Phase 2	Completed	10
Muscle Injury	Peter C Belafsky	University of California, Davis	Phase 1/2	Recruiting	62
Immune Disease	DR Jonathan Benjamin	ImmPACT-Bio, Inc.	Phase 1/2	Launching	N/A
Cystinosis Kidney Failure	Dr. Stephanie Cherqui	University of California, San Diego	Phase 1/2	Active, not recruiting	6
HIV/AIDS Immune Disease	Steven G. Deeks	University of California, San Francisco	Phase 1/2	Recruiting	18
Developmental Disorders Spina Bifida	Dr. Diana L. Farmer	University of California, Davis	Phase 2	Recruiting	55
Immune Disease Severe Combined Immunodeficiency, X-linked (X-SCID)	Stephen Gottschalk	St. Jude Children’s Research Hospital	Phase 1/2	Suspended	28
Bone or Cartilage Disease Hearing Loss Intellectual Disability Metabolic Disorders Vision Loss	Dr Robert Hayes	Immusoft Corporation	Phase 1	Launching	N/A
Arthritis Osteoarthritis	Dr. Kristen A Johnson	Calibr	Phase 1	Completed	60
Neurological Disorders Other	Prof. Olivia Kim-McManus	University of California, San Diego	Phase 1/2	Launching	N/A
Pulmonary Hypertension Vascular Disease	Dr. Michael I Lewis	Cedars-Sinai Medical Center	Phase 1/2	Completed	26
Immune Disease Pediatrics Severe Combined Immunodeficiency, X-linked (X-SCID)	Dr. Judith A Shizuru Wendy Pang	Stanford University Jasper Therapeutics, Inc.	Phase 1/2	Recruiting	40
Immune Disease Leukocyte Adhesion Deficiency	Dr. Kinnari Patel	Rocket Pharmaceuticals, Inc.	Phase 1/2	Completed	9
Danon Disease Pediatrics	Dr. Jonathan Schwartz	Rocket Pharmaceuticals, Inc.	Phase 2	Launching	N/A
Solid Tumors	Dr. Dennis J Slamon	University of California, Los Angeles	Phase 1	Completed	46
Lupus, Systemic Lupus Erythematosus (SLE)	Bob Valamehr	Fate Therapeutics, Inc.	Phase 1	Launching	N/A
COVID-19 Respiratory Disorders	William van der Touw	Celularity Inc.	Phase 1/2	Unknown status	86
Blood Cancer Solid Tumors	Dr. Irving L Weissman MD	Stanford University	Phase 1	Completed	88
Bladder or Urinary Tract Disorder	James Yoo	Wake Forest University Health Sciences	Phase 1	Not yet recruiting	10
COVID-19 Respiratory Disorders	Prof. John A Zaia	City of Hope, Beckman Research Institute	Phase 1	Launching	N/A