CIRM Funded Clinical Trials

A Phase I Open Label Study to Evaluate the Safety and Tolerability of ISP-001 in Patients with Mucopolysaccharidosis Type 1

Disease Area:
Bone or Cartilage Disease, Hearing Loss, Intellectual Disability, Metabolic Disorders, Vision Loss
CIRM Grant:
CLIN2-14416 (Active)
Award Value:
Trial Sponsor:
Immusoft Corporation
Trial Stage:
Phase 1
Trial Status:
Targeted Enrollment:

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