CIRM Clinical Trials

Through its strategic funding of clinical trials, CIRM helps advance innovative stem cell and gene therapy discoveries toward future treatments for patients.

CIRM funds clinical trials across a broad range of diseases and conditions that include rare and genetic disorders, treatment-resistant and refractory diseases, and many forms of cancer. Our involvement in the clinical trial process is vital to transforming potential treatments into available therapies by accelerating pathways to commercialization.

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CIRM-Funded Clinical Trials

Photo Credit: UCLA Broad Stem Cell Research Center

Funding Opportunities

Visit our Funding Opportunities page to apply for clinical trial research funding.

Disease AreasInvestigatorOrganizationPhaseTrial StatusTarget EnrollmentDetail
Age-related macular degeneration Mark Salman Humayun University of Southern California Phase 1 Closed 16
Age-related macular degeneration Jane Stephanie Lebkowski Regenerative Patch Technologies LLC Phase 2 Recruiting N/A
Age-related macular degeneration Dr. Jeffrey H Stern Luxa Biotechnology Phase 1/2 Launching N/A
Bone or Cartilage Disease
Hearing Loss
Intellectual Disability
Metabolic Disorders
Vision Loss
Dr Robert Hayes Immusoft Corporation Phase 1 Launching N/A
Corneal Damage Dr. Sophie X Deng University of California, Los Angeles Phase 1 Recruiting 20
Corneal Damage R. Kim Brazzell Combangio, Inc. Phase 2 Launching N/A
Retinitis Pigmentosa Dr. Henry John Klassen University of California, Irvine Phase 1/2 Completed 28
Retinitis Pigmentosa Henry John Klassen jCyte, Inc. Phase 2 Completed 84
Retinitis Pigmentosa Professor Clive Niels Svendsen Cedars-Sinai Medical Center Phase 1 Recruiting 16
Retinitis Pigmentosa Henry John Klassen jCyte, Inc. Phase 2 Completed 84
Retinitis Pigmentosa Paul Bresge Ray Therapeutics, INC Phase 1 Recruiting N/A