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2025 |
Sci Rep |
| ADMET-AI Enables Interpretable Predictions of Drug-Induced Cardiotoxicity. |
2025 |
Circulation |
| Allogeneic CD33-directed CAR-NKT cells for the treatment of bone marrow-resident myeloid malignancies. |
2025 |
Nat Commun |
| Derivation and Characterization of Isogenic OPA1 Mutant and Control Human Pluripotent Stem Cell Lines. |
2025 |
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2025 |
Nat Protoc |
| Genome editing with programmable base editors in human cells. |
2025 |
Methods Enzymol |
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2025 |
Nat Commun |
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2024 |
Exp Neurol |
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2024 |
J Clin Invest |
| A framework for N-of-1 trials of individualized gene-targeted therapies for genetic diseases. |
2024 |
Nat Commun |
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2024 |
Mol Ther Methods Clin Dev |
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2024 |
bioRxiv |
| A therapy for suppressing canonical and noncanonical SARS-CoV-2 viral entry and an intrinsic intrapulmonary inflammatory response. |
2024 |
Proc Natl Acad Sci U S A |
| Acid-degradable lipid nanoparticles enhance the delivery of mRNA. |
2024 |
Nat Nanotechnol |
| AMPK Drives both Glycolytic and Oxidative Metabolism in Murine and Human T Cells During Graft-versus-host Disease. |
2024 |
Blood Adv |
| An age-progressive platelet differentiation path from hematopoietic stem cells causes exacerbated thrombosis. |
2024 |
Cell |
| An Endothelial Cell Is Not Simply an Endothelial Cell. |
2024 |
Stem Cells Dev |
| An improved method for generating human spinal cord neural stem cells. |
2024 |
Exp Neurol |
| Antigen-Specific T Cell Receptor Discovery for Treating Progressive Multifocal Leukoencephalopathy. |
2024 |
bioRxiv |
| Antisense oligonucleotide therapy in an individual with KIF1A-associated neurological disorder. |
2024 |
Nat Med |
| Antiviral cellular therapy for enhancing T-cell reconstitution before or after hematopoietic stem cell transplantation (ACES): a two-arm, open label phase II interventional trial of pediatric patients with risk factor assessment. |
2024 |
Nat Commun |
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2024 |
Nat Commun |
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2024 |
J Biomed Mater Res A |
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2024 |
J Mol Endocrinol |
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2024 |
Cell Stem Cell |
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2024 |
Biomaterials |
| Defining metabolic flexibility in hair follicle stem cell induced squamous cell carcinoma. |
2024 |
Sci Adv |
| Disease modeling and pharmacological rescue of autosomal dominant retinitis pigmentosa associated with RHO copy number variation. |
2024 |
Elife |
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2024 |
Sci Adv |
| Engineered Protein Hydrogels as Biomimetic Cellular Scaffolds. |
2024 |
Adv Mater |
| Engineering allorejection-resistant CAR-NKT cells from hematopoietic stem cells for off-the-shelf cancer immunotherapy. |
2024 |
Mol Ther |
| Fatty acid oxidation in immune function. |
2024 |
Front Immunol |
| Frontiers in CAR-T cell therapy for autoimmune diseases. |
2024 |
Trends Pharmacol Sci |
| Functional outcome of the anterior vaginal wall in a pelvic surgery injury rat model after treatment with stem cell-derived progenitors of smooth muscle cells. |
2024 |
Stem Cell Res Ther |
| Gene editing improves endoplasmic reticulum-mitochondrial contacts and unfolded protein response in Friedreich’s ataxia iPSC-derived neurons. |
2024 |
Front Pharmacol |
| Generation of ‘semi-guided’ cortical organoids with complex neural oscillations. |
2024 |
Nat Protoc |
| Generation of allogeneic CAR-NKT cells from hematopoietic stem and progenitor cells using a clinically guided culture method. |
2024 |
Nat Biotechnol |
| Generation of antigen-specific mature T cells from RAG1(-/-)RAG2(-/-)B2M(-/-) stem cells by engineering their microenvironment. |
2024 |
Nat Biomed Eng |
| Harnessing Biomaterials to Amplify Immunity in Aged Mice through T Memory Stem Cells. |
2024 |
ACS Nano |
| Increased mitochondrial mutation heteroplasmy induces aging phenotypes in pluripotent stem cells and their differentiated progeny. |
2024 |
Aging Cell |
| Inhibition of Pyruvate Oxidation Diminishes Melanoma Progression. |
2024 |
J Invest Dermatol |
| Lentiviral vectors for precise expression to treat X-linked lymphoproliferative disease. |
2024 |
Mol Ther Methods Clin Dev |
| Locoregional delivery of IL-13Ralpha2-targeting CAR-T cells in recurrent high-grade glioma: a phase 1 trial. |
2024 |
Nat Med |
| Modeling Cortical Versus Hippocampal Network Dysfunction in a Human Brain Assembloid Model of Epilepsy and Intellectual Disability. |
2024 |
bioRxiv |
| Molecular profiling of human blastocysts reveals primitive endoderm defects among embryos of decreased implantation potential. |
2024 |
Cell Rep |
| Multi-lineage heart-chip models drug cardiotoxicity and enhances maturation of human stem cell-derived cardiovascular cells. |
2024 |
Lab Chip |
| Netrin1 patterns the dorsal spinal cord through modulation of Bmp signaling. |
2024 |
Cell Rep |
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2024 |
Croat Med J |
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2024 |
J Biol Chem |
| Recent developments in translational imaging of in vivo gene therapy outcomes. |
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Mol Ther |
