CIRM Clinical Trials

Through its strategic funding of clinical trials, CIRM helps advance innovative stem cell and gene therapy discoveries toward future treatments for patients.

CIRM funds clinical trials across a broad range of diseases and conditions that include rare and genetic disorders, treatment-resistant and refractory diseases, and many forms of cancer. Our involvement in the clinical trial process is vital to transforming potential treatments into available therapies by accelerating pathways to commercialization. Visit our Funding Opportunities page to apply for clinical trial research funding.

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CIRM-Funded Clinical Trials

Disease AreasInvestigatorOrganizationPhaseTrial StatusTarget EnrollmentDetail
Amyotrophic Lateral Sclerosis Dr. Ralph Kern BrainStorm Cell Therapeutics Phase 3 Completed 196
Stroke Dr. Bijan Nejadnik SanBio, Inc. Phase 2 Completed 163
Neurological Disorders Amit Etkin Alto Neuroscience Phase 2 Launching N/A
Developmental Disorders
Spina Bifida
Dr. Diana L. Farmer University of California, Davis Phase 2 Recruiting 55
Huntington's Disease Dr. Vicki Wheelock University of California, Davis Phase 1/2 Completed 29
Spinal Cord Injury Francois Binette Lineage Cell Therapeutics, Inc. Phase 1/2 Completed 25
Neurological Disorders
Other
Prof. Olivia Kim-McManus University of California, San Diego Phase 1/2 Launching N/A
Amyotrophic Lateral Sclerosis Professor Clive Niels Svendsen Cedars-Sinai Medical Center Phase 1/2 Completed 18
Spinal Cord Injury Dr. Jane Stephanie Lebkowski Dr. Geron Corporation Phase 1 Completed 5
Bone or Cartilage Disease
Hearing Loss
Intellectual Disability
Metabolic Disorders
Vision Loss
Dr Robert Hayes Immusoft Corporation Phase 1 Launching N/A
Parkinson's Disease Dr. Edward Wirth III Aspen Neuroscience Phase 1 Launching N/A
Parkinson's Disease Krystof S. Bankiewicz Brain Neurotherapy Bio Phase 1 Active, not recruiting 11
Amyotrophic Lateral Sclerosis Clive Svendsen Cedars-Sinai Medical Center Phase 1 Launching N/A
Stroke Dr. Gary Steinberg Stanford University Phase 1 Recruiting 30
Epilepsy Dr. Cory R Nicholas Neurona Therapeutics Phase 1 Recruiting 40