Disease Focus: Developmental Disorders


Spotlight on Batten Disease: Seminar by Stephen Huhn, M.D., F.A.C.S., F.A.A.P.

Stephen Huhn, M.D., F.A.C.S., F.A.A.P. spoke at the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board meeting on August 13, 2008. Huhn summarized the biology of Batten disease and discussed the clinical trial that is currently underway.  Huhn is Vice President and Head of the Neural Program at Stem Cells, […]

Spotlight on Batten Disease: Seminar by Ann Tsukamoto, Ph.D.

Ann Tsukamoto, Ph.D. spoke at the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board meeting on August 13, 2008. Tsukamoto reviewed the process of isolating, characterizing, and preparing human central nervous stem cells for use in a clinical trial designed to test a Batten disease cell-based therapy. Tsukamoto is the […]

Spotlight on Batten Disease: Seminar by Tony Ferradino

Tony Ferrandino spoke at the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board Meeting on August 13, 2008. Ferrandino’s son, Drew, was diagnosed with Batten disease in January 2007. Ferrandino spoke about his family’s journey to identify Drew’s condition and to seek out a treatment. Drew is enrolled in a […]