Disease Focus: Developmental Disorders
Anjana Nityanandam, Scripps – CIRM Stem Cell #SciencePitch
Gage Crump, USC – CIRM Stem Cell #SciencePitch
Produced by the University of Southern California
Joshua’s Heart Story: Pediatric Heart Disease and the Promise of Stem Cell Advances
The day before 9/11, just four months pregnant, Mary Goulart and her husband learned through ultrasounds that their baby had several heart defects including a missing left ventricle. After birth, baby Joshua endured three open-heart surgeries and a massive stroke. Through years of various therapies and true determination, Joshua met his challenges with many accomplishments. […]
Video: Stem Cell Banking – The Perspective of an iPS Donor Family
“Your twin daughters have an extremely rare, fatal disease called Niemann Pick Type C and there’s nothing you can do for them”. Those were the devastating words that Chris Hempel and her husband first heard in 2007. Rather than just give in to this fate, the Hempels are proactively engaging researchers to try to save […]
Spotlight on Batten Disease: Welcoming Remarks
Robert Klein, J.D. and Ed Penhoet, Ph.D. gave the welcoming remarks for the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board meeting on August 13, 2008. Klein is Chair of the CIRM Governing Board and President of Klein Financial Corporation. Penhoet is a member of the CIRM Governing Board and […]
Spotlight on Batten Disease: Seminar by Stephen Huhn, M.D., F.A.C.S., F.A.A.P.
Stephen Huhn, M.D., F.A.C.S., F.A.A.P. spoke at the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board meeting on August 13, 2008. Huhn summarized the biology of Batten disease and discussed the clinical trial that is currently underway. Huhn is Vice President and Head of the Neural Program at Stem Cells, […]
Spotlight on Batten Disease: Seminar by Ann Tsukamoto, Ph.D.
Ann Tsukamoto, Ph.D. spoke at the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board meeting on August 13, 2008. Tsukamoto reviewed the process of isolating, characterizing, and preparing human central nervous stem cells for use in a clinical trial designed to test a Batten disease cell-based therapy. Tsukamoto is the […]
Spotlight on Batten Disease: Seminar by Tony Ferradino
Tony Ferrandino spoke at the “Spotlight on Batten Disease,” an educational event presented at the CIRM Governing Board Meeting on August 13, 2008. Ferrandino’s son, Drew, was diagnosed with Batten disease in January 2007. Ferrandino spoke about his family’s journey to identify Drew’s condition and to seek out a treatment. Drew is enrolled in a […]