Funding Clinical Trials

Funding Clinical Trials

Our Agency funds clinical trials testing promising stem cell or gene therapies for currently incurable diseases or disorders to help patients with unmet medical needs. For basic information about stem cell trials, visit our Clinical Trials 101 page. For a list of clinical trials that are a result of early-stage CIRM grants click here.

CIRM Clinical Dashboard

Disease Areas Investigator Organization Phasesort descending Trial Status Targeted Enrollment Detail
  • Alpha Thalassemia Major
 Tippi MacKenzie University of California, San Francisco Phase 1 Enrolling by invitation 10
Donald Kohn University of California, Los Angeles Phase 1 Recruiting 6
De-Fu Zeng City of Hope, Beckman Research Institute Phase 1 Active, not recruiting 3
  • Severe Combined Immunodeficiency, Artemis deficient (ART-SCID)
 Morton Cowan University of California, San Francisco Phase 1 Recruiting 25
Pierre Caudrelier ExCellThera Inc. Phase 1 Withdrawn N/A
Mark Walters University of California, San Francisco Phase 1 Launching N/A
  • IPEX Syndrome
 Rosa Bacchetta Stanford University Phase 1 Recruiting 36
  • Immune Disease
  • Pediatrics
  • X-linked Chronic Granulomatous Disease
 Donald Kohn University of California, Los Angeles Phase 1/2 Active, not recruiting 16
Stephen Gottschalk St. Jude Children's Research Hospital Phase 1/2 Recruiting 28
Judith Shizuru Stanford University Phase 1/2 Recruiting 40
Michael Pulsipher Children's Hospital of Los Angeles Phase 1/2 Active, not recruiting 60
  • Beta Thalassemia
 Bettina Cockroft Sangamo BioSciences, Inc. Phase 1/2 Completed 5
  • Immune Disease
  • Leukocyte Adhesion Deficiency
 Kinnari Patel Rocket Pharmaceuticals, Inc. Phase 1/2 Active, not recruiting 9
  • Anemia
  • Bone Marrow Transplant and Viral Infection
 Alice Bertaina Stanford University Phase 1/2 Launching N/A
Donald Kohn University of California, Los Angeles Phase 2 Completed 10
David Williams Boston Children's Hospital Phase 2 Active, not recruiting 10
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