Funding Clinical Trials

Funding Clinical Trials

Our Agency funds clinical trials testing promising stem cell or gene therapies for currently incurable diseases or disorders to help patients with unmet medical needs. For basic information about stem cell trials, visit our Clinical Trials 101 page. For a list of clinical trials that are a result of early-stage CIRM grants click here.

CIRM Clinical Dashboard

Disease Areas Investigator Organization Phase Trial Statussort descending Targeted Enrollment Detail
  • Immune Disease
  • Pediatrics
  • X-linked Chronic Granulomatous Disease
 Donald Kohn University of California, Los Angeles Phase 1/2 Active, not recruiting 16
Michael Pulsipher Children's Hospital of Los Angeles Phase 1/2 Active, not recruiting 60
De-Fu Zeng City of Hope, Beckman Research Institute Phase 1 Active, not recruiting 3
  • Immune Disease
  • Leukocyte Adhesion Deficiency
 Kinnari Patel Rocket Pharmaceuticals, Inc. Phase 1/2 Active, not recruiting 9
David Williams Boston Children's Hospital Phase 2 Active, not recruiting 10
Donald Kohn University of California, Los Angeles Phase 2 Completed 10
  • Beta Thalassemia
 Bettina Cockroft Sangamo BioSciences, Inc. Phase 1/2 Completed 5
  • Alpha Thalassemia Major
 Tippi MacKenzie University of California, San Francisco Phase 1 Enrolling by invitation 10
  • Anemia
  • Bone Marrow Transplant and Viral Infection
 Alice Bertaina Stanford University Phase 1/2 Launching N/A
Mark Walters University of California, San Francisco Phase 1 Launching N/A
Donald Kohn University of California, Los Angeles Phase 1 Recruiting 6
Stephen Gottschalk St. Jude Children's Research Hospital Phase 1/2 Recruiting 28
Judith Shizuru Stanford University Phase 1/2 Recruiting 40
  • Severe Combined Immunodeficiency, Artemis deficient (ART-SCID)
 Morton Cowan University of California, San Francisco Phase 1 Recruiting 25
  • IPEX Syndrome
 Rosa Bacchetta Stanford University Phase 1 Recruiting 36
Pierre Caudrelier ExCellThera Inc. Phase 1 Withdrawn N/A
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