Funding Clinical Trials

Funding Clinical Trials

Our Agency funds clinical trials testing promising stem cell or gene therapies for currently incurable diseases or disorders to help patients with unmet medical needs. For basic information about stem cell trials, visit our Clinical Trials 101 page. For a list of clinical trials that are a result of early-stage CIRM grants click here.

CIRM Clinical Dashboard

Disease Areas Investigatorsort descending Organization Phase Trial Status Targeted Enrollment Detail
  • IPEX Syndrome
 Rosa Bacchetta Stanford University Phase 1 Recruiting 36
  • Anemia
  • Bone Marrow Transplant and Viral Infection
 Alice Bertaina Stanford University Phase 1/2 Launching N/A
Pierre Caudrelier ExCellThera Inc. Phase 1 Withdrawn N/A
  • Beta Thalassemia
 Bettina Cockroft Sangamo BioSciences, Inc. Phase 1/2 Completed 5
  • Severe Combined Immunodeficiency, Artemis deficient (ART-SCID)
 Morton Cowan University of California, San Francisco Phase 1 Recruiting 25
Stephen Gottschalk St. Jude Children's Research Hospital Phase 1/2 Recruiting 28
  • Immune Disease
  • Pediatrics
  • X-linked Chronic Granulomatous Disease
 Donald Kohn University of California, Los Angeles Phase 1/2 Active, not recruiting 16
Donald Kohn University of California, Los Angeles Phase 1 Recruiting 6
Donald Kohn University of California, Los Angeles Phase 2 Completed 10
  • Alpha Thalassemia Major
 Tippi MacKenzie University of California, San Francisco Phase 1 Enrolling by invitation 10
  • Immune Disease
  • Leukocyte Adhesion Deficiency
 Kinnari Patel Rocket Pharmaceuticals, Inc. Phase 1/2 Active, not recruiting 9
Michael Pulsipher Children's Hospital of Los Angeles Phase 1/2 Active, not recruiting 60
Judith Shizuru Stanford University Phase 1/2 Recruiting 40
Mark Walters University of California, San Francisco Phase 1 Launching N/A
David Williams Boston Children's Hospital Phase 2 Active, not recruiting 10
De-Fu Zeng City of Hope, Beckman Research Institute Phase 1 Active, not recruiting 3
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