Funding Clinical Trials

Funding Clinical Trials

Our Agency funds clinical trials testing promising stem cell or gene therapies for currently incurable diseases or disorders to help patients with unmet medical needs. For basic information about stem cell trials, visit our Clinical Trials 101 page. For a list of clinical trials that are a result of early-stage CIRM grants click here.

CIRM Clinical Dashboard

Disease Areassort descending Investigator Organization Phase Trial Status Targeted Enrollment Detail
  • Alpha Thalassemia Major
 Tippi MacKenzie University of California, San Francisco Phase 1 Enrolling by invitation 10
  • Anemia
  • Bone Marrow Transplant and Viral Infection
 Alice Bertaina Stanford University Phase 1/2 Launching N/A
  • Anemia
 Matthew Porteus Stanford University Phase 1/2 Launching N/A
  • Beta Thalassemia
 Bettina Cockroft Sangamo BioSciences, Inc. Phase 1/2 Completed 5
Michael Pulsipher Children's Hospital of Los Angeles Phase 1/2 Active, not recruiting 60
Donald Kohn University of California, Los Angeles Phase 2 Completed 10
  • Immune Disease
  • Pediatrics
  • X-linked Chronic Granulomatous Disease
 Donald Kohn University of California, Los Angeles Phase 1/2 Active, not recruiting 16
Stephen Gottschalk St. Jude Children's Research Hospital Phase 1/2 Suspended 28
Judith Shizuru Stanford University Phase 1/2 Recruiting 40
  • Immune Disease
  • Leukocyte Adhesion Deficiency
 Kinnari Patel Rocket Pharmaceuticals, Inc. Phase 1/2 Active, not recruiting 9
  • IPEX Syndrome
 Rosa Bacchetta Stanford University Phase 1 Recruiting 36
Donald Kohn University of California, Los Angeles Phase 1 Recruiting 6
  • Severe Combined Immunodeficiency, Artemis deficient (ART-SCID)
 Morton Cowan University of California, San Francisco Phase 1 Recruiting 25
De-Fu Zeng City of Hope, Beckman Research Institute Phase 1 Active, not recruiting 3
Pierre Caudrelier ExCellThera Inc. Phase 1 Withdrawn N/A
David Williams Boston Children's Hospital Phase 2 Active, not recruiting 10
Mark Walters University of California, San Francisco Phase 1 Launching N/A
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