A targeted antisense oligonucleotide therapeutic strategy for Timothy syndrome Post author: Post published:January 24, 2026 Post category: Continue ReadingA targeted antisense oligonucleotide therapeutic strategy for Timothy syndrome
GlyTR2 CAR T cell translation: safe pan-cancer killing via velcro-like density-dependent targeting of cancer glycans Post author: Post published:January 24, 2026 Post category: Continue ReadingGlyTR2 CAR T cell translation: safe pan-cancer killing via velcro-like density-dependent targeting of cancer glycans
FM-IL2 CAR T cells for Pancreatic Cancer Post author: Post published:January 24, 2026 Post category: Continue ReadingFM-IL2 CAR T cells for Pancreatic Cancer
Lep001 – gene therapy for the treatment of congenital lipodystrophy Post author: Post published:January 24, 2026 Post category: Continue ReadingLep001 – gene therapy for the treatment of congenital lipodystrophy
Development of an off-the-shelf iPSC derived CAR T cell therapy for the treatment of solid tumors Post author: Post published:January 24, 2026 Post category: Continue ReadingDevelopment of an off-the-shelf iPSC derived CAR T cell therapy for the treatment of solid tumors
Development of an AAV Epigenetic Gene Therapy for Gain-of-Function SCN9A Disorders and Chronic Pain Post author: Post published:January 24, 2026 Post category: Continue ReadingDevelopment of an AAV Epigenetic Gene Therapy for Gain-of-Function SCN9A Disorders and Chronic Pain
Evaluation of an ex vivo lentiviral gene therapy for the treatment of Angelman syndrome Post author: Post published:January 24, 2026 Post category: Continue ReadingEvaluation of an ex vivo lentiviral gene therapy for the treatment of Angelman syndrome
A Novel Gene Therapy to Target Glioblastoma via Custom-Engineered Adenovirus-Associated Viral Vectors Post author: Post published:January 24, 2026 Post category: Continue ReadingA Novel Gene Therapy to Target Glioblastoma via Custom-Engineered Adenovirus-Associated Viral Vectors
Parkin Gene Therapy for Parkinson’s Disease Post author: Post published:January 24, 2026 Post category: Continue ReadingParkin Gene Therapy for Parkinson’s Disease
Hematopoietic Stem Cell Gene Therapy for Alpha Thalassemia Post author: Post published:January 24, 2026 Post category: Continue ReadingHematopoietic Stem Cell Gene Therapy for Alpha Thalassemia