Skip to content
CA.gov logo in white
  • Grants Management System
  • CIRM Hub Portal
  • Contact
  • About
    • Our Mission
    • Our Impact
    • Our Governing Board
    • Strategic Goals
    • Our Team
    • Annual Reports
  • For Researchers
    • Funding Opportunities
    • Information for Applicants
    • Researcher Resources
    • Our Review Process
  • Our Programs
    • Grants Dashboard
    • Research and Development
    • Education and Training
    • Patient Access
  • Patient Resources
    • Stem Cell and Genetic Research
    • From Bench to Bedside
    • Community Outreach
    • Clinical Trials
    • Community Stories
  • News and Events
    • Press Releases
    • Public Meetings
    • Blog
    • Webinars and Workshops
  • About
    • Our Mission
    • Our Impact
    • Our Governing Board
    • Strategic Goals
    • Our Team
    • Annual Reports
  • For Researchers
    • Funding Opportunities
    • Information for Applicants
    • Researcher Resources
    • Our Review Process
  • Our Programs
    • Grants Dashboard
    • Research and Development
    • Education and Training
    • Patient Access
  • Patient Resources
    • Stem Cell and Genetic Research
    • From Bench to Bedside
    • Community Outreach
    • Clinical Trials
    • Community Stories
  • News and Events
    • Press Releases
    • Public Meetings
    • Blog
    • Webinars and Workshops

MicroRNAs in Human Stem Cell Differentiation and Mental Disorders

  • Post author:
  • Post published:May 19, 2026
  • Post category:

Many mental disorders are closely associated with problems that occur during brain development in early life. For instance, by 2 years of age, autistic children have larger brains than normal…

Continue ReadingMicroRNAs in Human Stem Cell Differentiation and Mental Disorders

Lep001 – gene therapy for the treatment of congenital lipodystrophy

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Continue ReadingLep001 – gene therapy for the treatment of congenital lipodystrophy

2016 Gordon Research Conference on Craniofacial Morphogenesis and Tissue Regeneration

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Continue Reading2016 Gordon Research Conference on Craniofacial Morphogenesis and Tissue Regeneration

Phase 1/2 Study to Evaluate the Safety, Tolerability, and Efficacy of MZ-1866, a gene therapy for Pitt Hopkins Syndrome

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Continue ReadingPhase 1/2 Study to Evaluate the Safety, Tolerability, and Efficacy of MZ-1866, a gene therapy for Pitt Hopkins Syndrome

Phase I/II Clinical Trial for CMT4J

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Continue ReadingPhase I/II Clinical Trial for CMT4J

The CuRe Trial: Cellular Therapy for In Utero Repair of Myelomeningocele

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Therapeutic Candidate or Device Allogeneic Placenta-derived Mesenchymal Stem Cells Seeded on Cook Biodesign® Dural Graft Extracellular Matrix (PMSC-ECM) Indication Myelomeningocele (MMC) -or Spina Bifida -diagnosed prenatally Therapeutic Mechanism Placenta-derived mesenchymal…

Continue ReadingThe CuRe Trial: Cellular Therapy for In Utero Repair of Myelomeningocele

Pre-Clinical To Clinical Gene Therapy Development For CMT4J

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Therapeutic Candidate or Device AAV9 Gene Therapy For An Ultra-Rare Disease Called CMT4J Indication CMT4J or the FIG4 Gene Therapeutic Mechanism Gene Therapy through an Intrathecal One-Time Injection Unmet Medical…

Continue ReadingPre-Clinical To Clinical Gene Therapy Development For CMT4J

Stem Cells Craniofacial Development and Disease

  • Post author:
  • Post published:May 18, 2026
  • Post category:

Continue ReadingStem Cells Craniofacial Development and Disease

Phase 1/2 Study to Evaluate the Safety, Tolerability, and Efficacy of MZ-1866, a gene therapy for Pitt Hopkins Syndrome

  • Post author:
  • Post published:May 17, 2026
  • Post category:

Continue ReadingPhase 1/2 Study to Evaluate the Safety, Tolerability, and Efficacy of MZ-1866, a gene therapy for Pitt Hopkins Syndrome

Phase I/II Clinical Trial for CMT4J

  • Post author:
  • Post published:May 17, 2026
  • Post category:

Continue ReadingPhase I/II Clinical Trial for CMT4J
  • 1
  • 2
  • 3
  • 4
  • Go to the next page
  • Careers
  • Administrative & Financials
  • Accessibility

Subscribe to Receive CIRM News

Get the latest CIRM news, information on upcoming meetings, and funding opportunities delivered to your inbox. 

Sign Up
Facebook-f X-twitter Instagram Linkedin Youtube
  • Privacy Policy
  • ©2025 California Institute for Regenerative Medicine
  • Media Guidelines
  • Contact Us