RAPA-501 Therapy of ALS Expanded Access Protocol Post author: Post published:April 20, 2026 Post category: Continue ReadingRAPA-501 Therapy of ALS Expanded Access Protocol
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Gene Therapy for Cardiomyopathy Associated With Friedreich’s Ataxia Post author: Post published:April 20, 2026 Post category: Continue ReadingGene Therapy for Cardiomyopathy Associated With Friedreich’s Ataxia
A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients Post author: Post published:April 20, 2026 Post category: Continue ReadingA Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients
Cellular Therapy for In Utero Repair of Myelomeningocele – The CuRe Trial Post author: Post published:April 20, 2026 Post category: Continue ReadingCellular Therapy for In Utero Repair of Myelomeningocele – The CuRe Trial
A Safety and Tolerability Study of Neural Stem Cells (NR1) in Subjects With Chronic Ischemic Subcortical Stroke (ISS) Post author: Post published:April 20, 2026 Post category: Continue ReadingA Safety and Tolerability Study of Neural Stem Cells (NR1) in Subjects With Chronic Ischemic Subcortical Stroke (ISS)
Autologous Muscle Derived Cells for Treatment of Tongue Dysphagia Post author: Post published:April 20, 2026 Post category: Continue ReadingAutologous Muscle Derived Cells for Treatment of Tongue Dysphagia
Intracranial Genetically Modified Immune Cells (TGFβR2KO/IL13Rα2 CAR T-Cells) for the Treatment of Recurrent or Progressive Glioblastoma or Grade 3 or 4 IDH-Mutant Astrocytoma Post author: Post published:April 20, 2026 Post category: Continue ReadingIntracranial Genetically Modified Immune Cells (TGFβR2KO/IL13Rα2 CAR T-Cells) for the Treatment of Recurrent or Progressive Glioblastoma or Grade 3 or 4 IDH-Mutant Astrocytoma
Anti-EGFRvIII synNotch Receptor Induced Anti-EphA2/IL-13Ralpha2 CAR (E-SYNC) T Cells Post author: Post published:April 20, 2026 Post category: Continue ReadingAnti-EGFRvIII synNotch Receptor Induced Anti-EphA2/IL-13Ralpha2 CAR (E-SYNC) T Cells