Microglia replacement therapy for CSF1R-related Leukoencephalopathy

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TY1 and Semaglutide to Treat Cardiometabolic HFpEF

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CRISPR/Cas9-mediated gene editing of Hematopoietic stem and progenitor cells for Friedreich’s ataxia

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Noncoding RNA drug TY2 for arrhythmogenic cardiomyopathy

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Development of an AAV Epigenetic Gene Therapy for Intractable Chronic Pain Disorders

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Stem Cell-Based Cartilage Tissue Regeneration

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Autologous iPSC-derived progenitor smooth muscle cells for treatment of urinary incontinence

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COVID-19 Antiviral Therapy to Block Direct Cell Injury and Associated Tissue Damage

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Translational Candidate Berzosertib (VE-822), a safe drug candidate for treatment against COVID-19, will be investigated. Area of Impact The outcome of the proposed studies will have a significant health benefit…

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Purpose built cell engineering for rapid manufacturing of stem-like cell therapies

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Purification of Human Hematopoietic Stem Cells (HSCs) for Clinical Stem Cell Transplantation

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Translational Candidate Two new monoclonal antibodies anti-CD34 and anti-CD90, and protocols to purify cancer-free and/or T cell free human HSC for clinical transplantation. Area of Impact The development of hematopoietic…

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