Clinical Trial Stage Projects | University of California, San Francisco | Gene Therapy for Artemis-Deficient Severe Combined Immunodeficiency Using a Self-Inactivating Lentiviral Vector |
$14,999,999 |
Clinical Trial Stage Projects | University of California, San Francisco | Gene Transfer for Artemis-Deficient Severe Combined Immunodeficiency Using a Lentiviral Vector to Transduce Autologous CD34 Hematopoietic Stem Cells |
$12,000,000 |
Early Translational III | University of California, San Francisco | Gene Correction of Autologous Hematopoietic Stem Cells in Artemis Deficient SCID |
$3,862,367 |