Awards as PI
| Program Type | Institution | Grant Title | Award Value |
|---|---|---|---|
| Preclinical Development Awards | Stanford University | Pre-clinical development of gene correction therapy of hematopoietic stem cells for SCID-X1 | $874,877 |
| Quest - Discovery Stage Research Projects | Stanford University | Genome Editing to Correct Cystic Fibrosis Mutations in Airway Stem Cells | $1,968,456 |
| Late Stage Preclinical Projects | Stanford University | Genome Editing of Autologous Hematopoietic Stem Cells to Treat Sickle Cell Disease | $4,849,363 |
Total: $7,692,696.00 |
Publications
- Nat Med 2018 A high-fidelity Cas9 mutant delivered as a ribonucleoprotein complex enables efficient gene editing in human hematopoietic stem and progenitor cells. (PubMed: 30082871)
- Cell Stem Cell 2019 High-Efficiency, Selection-free Gene Repair in Airway Stem Cells from Cystic Fibrosis Patients Rescues CFTR Function in Differentiated Epithelia. (PubMed: 31839569)