Donald Kohn

Awards as PI

Program Type	Institution	Grant Title	Award Value
Quest - Discovery Stage Research Projects	University of California, Los Angeles	Hematopoietic Stem Cell Gene Therapy for X-linked Agammaglobulinemia	$219,230
Disease Team Research I	University of California, Los Angeles	Stem Cell Gene Therapy for Sickle Cell Disease	$8,833,695
Early Translational IV	University of California, Los Angeles	Beta-Globin Gene Correction of Sickle Cell Disease in Hematopoietic Stem Cells	$1,651,884
Disease Team Therapy Development III	University of California, Los Angeles	Clinical Trial of Stem Cell Gene Therapy for Sickle Cell Disease	$13,145,465
Clinical Trial Stage Projects	University of California, Los Angeles	A Phase I/II, Non Randomized, Multicenter, Open-Label Study of G1XCGD (Lentiviral Vector Transduced CD34+ Cells) in Patients With X-Linked Chronic Granulomatous Disease	$7,083,364
Conference II	University of California, Los Angeles	Primary Immune Deficiency Treatment Consortium (PIDTC) Annual Scientific Workshop	$29,807
Clinical Trial Stage Projects	University of California, Los Angeles	Efficacy and safety of cryopreserved autologous CD34+ HSC transduced with EFS lentiviral vector encoding for human ADA gene in ADA-SCID subjects	$5,827,000
Therapeutic Translational Research Projects	University of California, Los Angeles	Autologous MPO Knock-Out Hematopoietic Stem and Progenitor Cells for Pulmonary Arterial Hypertension	$5,207,434
			Total: $41,997,879.00

Stem Cell Gene Therapy for Sickle Cell Anemia - Donald Kohn	Stem Cell Cure for "Bubble Baby" Disease (SCID), Pioneered by UCLA's Don Kohn
Defeating Sickle Cell Disease with Stem Cells + Gene Therapy