Phase 1/2 Study to Evaluate the Safety, Tolerability, and Efficacy of MZ-1866, a gene therapy for Pitt Hopkins Syndrome

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Grant Award Details

Grant Number:
CLIN2-19119
Investigator(s):
Institution:
Type:
PI

Award Value:
$8,000,000
Status:
Pre-Active

Grant Application Details

Application Title:

Phase 1/2 Study to Evaluate the Safety, Tolerability, and Efficacy of MZ-1866, a gene therapy for Pitt Hopkins Syndrome