A Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients Post author: Post published:April 20, 2026 Post category: Continue ReadingA Single-Stage, Adaptive, Open-label, Dose Escalation Safety and Efficacy Study of AADC Deficiency in Pediatric Patients
Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis Post author: Post published:April 20, 2026 Post category: Continue ReadingStudy of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis
Pancreatic Islets and Parathyroid Gland Co-transplantation for Treatment of Type 1 Diabetes Post author: Post published:April 20, 2026 Post category: Continue ReadingPancreatic Islets and Parathyroid Gland Co-transplantation for Treatment of Type 1 Diabetes
ET140203 T Cells in Pediatric Subjects With Hepatoblastoma, HCN-NOS, or Hepatocellular Carcinoma Post author: Post published:April 20, 2026 Post category: Continue ReadingET140203 T Cells in Pediatric Subjects With Hepatoblastoma, HCN-NOS, or Hepatocellular Carcinoma
Treatment of Moderate to Severe Refractory Crohn’s Disease Post author: Post published:April 20, 2026 Post category: Continue ReadingTreatment of Moderate to Severe Refractory Crohn’s Disease
Autologous Muscle Derived Cells for Treatment of Tongue Dysphagia Post author: Post published:April 20, 2026 Post category: Continue ReadingAutologous Muscle Derived Cells for Treatment of Tongue Dysphagia
RESET-Myositis: An Open-Label Study to Evaluate the Safety and Efficacy of CABA-201 in Subjects With Active Idiopathic Inflammatory Myopathy or Juvenile Idiopathic Inflammatory Myopathy Post author: Post published:April 20, 2026 Post category: Continue ReadingRESET-Myositis: An Open-Label Study to Evaluate the Safety and Efficacy of CABA-201 in Subjects With Active Idiopathic Inflammatory Myopathy or Juvenile Idiopathic Inflammatory Myopathy
A Phase I/II Study to Evaluate AZD5851 in GPC3+ Advanced/Recurrent Hepatocellular Carcinoma Post author: Post published:April 20, 2026 Post category: Continue ReadingA Phase I/II Study to Evaluate AZD5851 in GPC3+ Advanced/Recurrent Hepatocellular Carcinoma
Safety and Efficacy of ALLO-316 in Subjects With Advanced or Metastatic Clear Cell Renal Cell Carcinoma Post author: Post published:April 20, 2026 Post category: Continue ReadingSafety and Efficacy of ALLO-316 in Subjects With Advanced or Metastatic Clear Cell Renal Cell Carcinoma
Anti-EGFRvIII synNotch Receptor Induced Anti-EphA2/IL-13Ralpha2 CAR (E-SYNC) T Cells Post author: Post published:April 20, 2026 Post category: Continue ReadingAnti-EGFRvIII synNotch Receptor Induced Anti-EphA2/IL-13Ralpha2 CAR (E-SYNC) T Cells
