Personalized antisense oligonucleotide therapy for rare pediatric genetic disease: SCN2A Post author: Post published:April 16, 2026 Post category: Continue ReadingPersonalized antisense oligonucleotide therapy for rare pediatric genetic disease: SCN2A
A Phase 2b Study of the Efficacy of a Novel Pro-Neurogenesis/Pro-Plasticity Drug for Bipolar Depression Using a Precision Psychiatry Approach Post author: Post published:April 16, 2026 Post category: Continue ReadingA Phase 2b Study of the Efficacy of a Novel Pro-Neurogenesis/Pro-Plasticity Drug for Bipolar Depression Using a Precision Psychiatry Approach
Late-stage development of AS-241, an UNC13A Targeting Antisense Oligonucleotide treatment for Amyotrophic Lateral Sclerosis, for IND-enabling studies Post author: Post published:April 16, 2026 Post category: Continue ReadingLate-stage development of AS-241, an UNC13A Targeting Antisense Oligonucleotide treatment for Amyotrophic Lateral Sclerosis, for IND-enabling studies
Microglia replacement therapy for CSF1R-related Leukoencephalopathy Post author: Post published:April 16, 2026 Post category: Continue ReadingMicroglia replacement therapy for CSF1R-related Leukoencephalopathy
CRISPR/Cas9-mediated gene editing of Hematopoietic stem and progenitor cells for Friedreich’s ataxia Post author: Post published:April 16, 2026 Post category: Continue ReadingCRISPR/Cas9-mediated gene editing of Hematopoietic stem and progenitor cells for Friedreich’s ataxia
Development of an AAV Epigenetic Gene Therapy for Intractable Chronic Pain Disorders Post author: Post published:April 16, 2026 Post category: Continue ReadingDevelopment of an AAV Epigenetic Gene Therapy for Intractable Chronic Pain Disorders
Dissecting cell-specific genetic and molecular drivers of amyotrophic lateral sclerosis for therapeutic insights Post author: Post published:April 16, 2026 Post category: Continue ReadingDissecting cell-specific genetic and molecular drivers of amyotrophic lateral sclerosis for therapeutic insights
Transplantation of human forebrain assembloids as a platform for therapeutic screening in neurodevelopmental disorders Post author: Post published:April 16, 2026 Post category: Continue ReadingTransplantation of human forebrain assembloids as a platform for therapeutic screening in neurodevelopmental disorders
Advancing Therapeutic Discovery Through Multimodal Analyses of Genetic and Cellular Mechanisms in Neuropsychiatric Disorders Post author: Post published:April 16, 2026 Post category: Continue ReadingAdvancing Therapeutic Discovery Through Multimodal Analyses of Genetic and Cellular Mechanisms in Neuropsychiatric Disorders
Reversing age-dependent neurodegeneration by elimination of RNA pollution Post author: Post published:April 16, 2026 Post category: Continue ReadingReversing age-dependent neurodegeneration by elimination of RNA pollution
