Translational Candidate Human hematopoietic stem cells that have been gene-corrected at the CD40L gene to treat patients with X-Linked Hyper-IgM Syndrome Area of Impact These studies will bring stem cell…
Translational Candidate The principal objective of this program is to bring a Cas9-based gene editing cure for sickle cell disease to the pre-IND stage of development. Area of Impact The…
Translational Candidate The principal objective of this program is to bring a Cas9-based gene editing cure for sickle cell disease to the pre-IND stage of development. Area of Impact The…
Clinical trials are risky and rely on brave pioneers who are willing to put their bodies on the line to test something never before tried in people. At its December…
Using a mix of science, humor and easy to understand language, this video describes sickle cell disease and a CIRM-funded clinical trial at UCLA that is testing a stem cell…
Dr. Robert Vescio spoke to CIRM's governing board to promote awareness about amyloidosis, a rare, often fatal disease caused by the abnormal deposit of proteins called amyloids in various tissues…
Michael York, star of films such as Cabaret, Logan's Run, and Austin Powers, spoke to the California stem cell agency governing board about his personal battle with amyloidosis, a rare,…
