Donald Kohn
Institution Name:
University of California, Los Angeles
Total Awards:
1
Award Value:
$10,156,925
Awards as PI
| Program Type | Institution | Grant Title | Award Value |
|---|---|---|---|
| Clinical Trial Stage Projects | University of California, Los Angeles | Efficacy and safety of cryopreserved autologous CD34+ HSC transduced with EFS lentiviral vector encoding for human ADA gene in ADA-SCID subjects | $10,156,925 |
Total: $10,156,925.00 |
Publications
- Biol Blood Marrow Transplant 2020 Busulfan Pharmacokinetics in Adenosine Deaminase-Deficient Severe Combined Immunodeficiency Gene Therapy. (PubMed: 32653625)
- J Clin Immunol 2021 Normal IgH Repertoire Diversity in an Infant with ADA Deficiency After Gene Therapy. (PubMed: 34184208)
- N Engl J Med 2021 Autologous Ex Vivo Lentiviral Gene Therapy for Adenosine Deaminase Deficiency. (PubMed: 33974366)